As of September 2022, 31 percent of medicines in the pre-registration phase of the R&D pipeline worldwide were orphan medicines. This graph illustrates the distribution of new medicines in the R&D pipeline worldwide, by therapeutic class.
Share of orphan medicines in the R&D pipeline worldwide as of 2022, by development phase
Figure includes 4,114 medicines in Phase I, 3,927 medicines in Phase II, 1,092 medicines in Phase II, and 165 medicines in the pre-registration phase.
Includes all pipeline medicines that are being developed for market in Canada, the United States, or geographic Europe (excluding Russia and Turkey). Orphan medicines were defined as pipeline medicines that have been granted an orphan designation by the US Food and Drug Administration (FDA) or the European Medicines Agency (EMA).
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PMPRB. (June 1, 2023). Share of orphan medicines in the R&D pipeline worldwide as of 2022, by development phase [Graph]. In Statista. Retrieved July 22, 2024, from https://www.statista.com/statistics/1335995/orphan-medicines-research-development-pipeline-by-phase-worldwide/
PMPRB. "Share of orphan medicines in the R&D pipeline worldwide as of 2022, by development phase." Chart. June 1, 2023. Statista. Accessed July 22, 2024. https://www.statista.com/statistics/1335995/orphan-medicines-research-development-pipeline-by-phase-worldwide/
PMPRB. (2023). Share of orphan medicines in the R&D pipeline worldwide as of 2022, by development phase. Statista. Statista Inc.. Accessed: July 22, 2024. https://www.statista.com/statistics/1335995/orphan-medicines-research-development-pipeline-by-phase-worldwide/
PMPRB. "Share of Orphan Medicines in The R&d Pipeline Worldwide as of 2022, by Development Phase." Statista, Statista Inc., 1 Jun 2023, https://www.statista.com/statistics/1335995/orphan-medicines-research-development-pipeline-by-phase-worldwide/
PMPRB, Share of orphan medicines in the R&D pipeline worldwide as of 2022, by development phase Statista, https://www.statista.com/statistics/1335995/orphan-medicines-research-development-pipeline-by-phase-worldwide/ (last visited July 22, 2024)
Share of orphan medicines in the R&D pipeline worldwide as of 2022, by development phase [Graph], PMPRB, June 1, 2023. [Online]. Available: https://www.statista.com/statistics/1335995/orphan-medicines-research-development-pipeline-by-phase-worldwide/
